For example, Biogen’s nusinersen, an ASO therapy for the fatal neuromuscular condition spinal muscular atrophy (SMA), can reduce by half the likelihood of death or the need for mechanical ...

When tested against conventional treatments, the personalized ASO therapy proved more effective at killing cancer cells and shrinking tumors, even in cases where the cancer had developed resistance to ...

HDOs consist of ASO DNA and complementary RNA strands ... and could potentially lead to organoid-based therapy for other digestive tract conditions, such as Crohn’s disease.

Vanda Pharmaceuticals Inc.’s VGT-1849A, a selective antisense oligonucleotide (ASO)-based JAK2 inhibitor, has been awarded ...

U.S. residents can learn more by visiting www.ultraclinicaltrials.com. GTX-102 is an investigational antisense oligonucleotide (ASO) therapy delivered via intrathecal administration and designed to ...

This extremely schizophrenic man was able to live an apparently normal life with their therapy. They published their work in Italian and later in English. Cerletti hoped to find a way to use the ...