Another important aspect of granulocyte transfusions is their use in patients with chronic granulomatous disease (CGD) undergoing hematopoietic cell transplantation (HCT) or gene therapy.
"This study highlights the potential for the gene therapy field to provide effective long-term therapies for chronic conditions, which currently require frequent treatments with painful and/or ...
The FDA cleared Prime Medicine’s investigational new drug (IND) application for PM359 for the treatment of chronic granulomatous ... field of next-generation gene editing.