Hereditary transthyretin (hATTR) amyloidosis is a rare progressive disease that is passed from parent to child. It is caused by a mutant form of the transthyretin (TTR) protein that can damage ...

This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...

Phase III HELIOS-B trial found that Amvuttra (vutrisiran) also preserved functional capacity and quality of life in patients ...

DNA analysis of TTR gene to detect or exclude hereditary transthyretin-related amyloidosis (ATTR). - Serum free light chain assay to detect low grade plasma-cell dyscrasia. - Mass spectrometry for ...

UAB researchers reveal how managing cardiovascular risk factors can mitigate heart failure risk in Black individuals carrying ...

Amyloidosis can be acquired or hereditary, localized or systemic, and is classified according to the fibril precursor protein. Local amyloid deposition occurs in the brain in Alzheimer's disease ...

The market will grow as a result of the increasing incidence of amyloidosis, technological advancements in diagnostics, ...

In the longest study of an RNAi therapeutic for any disease, patisiran treatment demonstrated modest improvements in patients ...

Share on Facebook. Opens in a new tab or window Share on Bluesky. Opens in a new tab or window Share on X. Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window Patisiran ...

Intellia Therapeutics Inc (NASDAQ:NTLA) outlined its strategic priorities for 2025, emphasizing the acceleration of ...

Early detection and treatment of hereditary transthyretin-related amyloidosis via genetic counseling are crucial. Yet, not all at-risk individuals seek genetic counseling, and management for ...