Researchers have identified early molecular changes in Rett syndrome that could lead to improved treatments for the condition. Scientists investigating the severe developmental disorder known as Rett ...
The Blue Bird Circle Rett Center at Baylor College of Medicine is composed of a multidisciplinary team of health professionals. Several BCM physicians are involved clinically at the Blue Bird Circle ...
The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died, but that won't cause the study to be halted. The FDA has allowed the ...
Taysha Gene Therapies' TSHA-102 tackles Rett syndrome’s root cause with its miniMECP2 transgene and scAAV delivery. So far, this is TSHA’s main value driver, and it appears safe and effective ...
If you haven't heard of Rett syndrome, it's probably because it's very rare. Affecting an estimated one in 12,000 baby girls born each year (and only rarely seen in boys), this genetic disorder ...