Altruism values for treatments of rare, severe pediatric diseases have not been estimated. This study found the altruism value for a hypothetical new Duchenne muscular dystrophy treatment to be $80 ...
(RTTNews) - MeiraGTx Holdings Plc. (MGTX), Wednesday announced that the U.S. Food and Drug Administration has granted the Rare Pediatric Disease Designation to its AAV8-RK-RetGC program for the ...