来自MSN5 天
How can awareness and treatment help manage thalassemia effectively?
Thalassemia is a hereditary blood disorder causing anaemia due to reduced haemoglobin production. Early detection, awareness, ...
Could a pill replace gene therapy for sickle cell disease? Research uncovers potential path ...
The new gene therapies for sickle cell disease—including the gene-editing treatment Casgevy, based on research at Boston ...
Thalassemia and Pregnancy: What Every Expecting Parent Needs to Know
Before planning pregnancy, please check your thalassemia status of wife and husband . Thalassemia is a preventable genetic ...
5 Of The Most Important Medical Breakthroughs Of 2024
From reprogrammed stem cells to next-generation gene editing, 2024 has seen some incredible developments with the potential to become new treatments.
Life-changing gene therapy to help local siblings
When you give to Light Up A Lawn, Light Up A Life, you are supporting programs like Nationwide Children's cutting-edge gene ...
The American Journal of Managed Care17 小时
New Evidence Highlights Stability of Lentiviral Gene Therapies
Researchers study long-term safety of lentiviral gene therapy in primates, finding no evidence of somatic mutations or ...
The New England Journal of Medicine9 天
The Silent Carrier of Beta Thalassemia
A family of Albanian descent had an unusual form of beta thalassemia. The father of two children with mild thalassemia major had normal red-cell morphology and normal levels of hemoglobins A 2 and ...
SHINE10 天
Locally-developed gene editing technology cures boy with serious blood disorder
The treatment CS-101 uses innovative transformer Base Editing (tBE) technology to help people with severe diseases such as ...
Business Wire13 天
Long-Term Follow-Up Data Continue to Support Beti-Cel as a Potentially Curative Gene ...
About ZYNTEGLO® (betibeglogene autotemcel) or beti-cel ZYNTEGLO is a first-in-class, one-time ex-vivo LVV gene therapy approved for the treatment of beta-thalassemia in adult and pediatric ...